• Clinical Trials for Pediatric Blood Disorders

    Dana-Farber/Boston Children’s Cancer and Blood Disorders Center is one of the world’s top pediatric research centers, and our scientific advances are propelled by unique clinical trials. Our scientists participate in large, multi-center research studies and also lead smaller, independent investigations.

    Clinical researchers at Dana-Farber/Boston Children's are committed to identifying new approaches to prevent, diagnose and treat childhood blood disorders. We currently have several blood disorders clinical trials underway, including studies to:

    • Determine if a drug used in cardiovascular stress testing can ease inflammation and reduce sickle cell symptoms
    • Reduce and prevent complications of hemophilia, especially blood-borne infections
    • Evaluate the safety and effectiveness of a new oral iron chelators to treat transfusional iron overload and a less potent androgen to treat Fanconi anemia and reduce side effects
    • Collect blood samples to study the immune system and look for markers of risk for immune thrombocytopenic purpura

    Search our current pediatric blood disorder clinical trials.

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  • Clinical Trial FAQs

    Get answers to common questions about clinical trials: What are clinical trials? Is a clinical trial the right choice for my child?