Childhood Conditions Treated with Stem Cell Transplant

At Dana-Farber/Boston Children's Cancer and Blood Disorders Center, stem cell transplant (also called bone marrow transplant) is used to treat many conditions affecting children and teens, including:

Cancers and Blood Disorders

• Acute lymphoblastic leukemia (ALL) — including relapsed ALL
• Acute myelogenous leukemia (AML)
• Aplastic anemia
• Brain tumors
• Chronic myelogenous leukemia
• Congenital sideroblastic anemia
• Dyskeratosis congenita
• Fanconi anemia
• Hodgkins lymphoma
• Juvenile myelomonocytic leukemia (JMML)
• Myelodysplastic syndrome
• Non-Hodgkins lymphoma
• Sickle cell disease
• Solid tumors such as neuroblastoma and Wilms’ tumor
• Thalassemia

Genetic Immunodeficiencies

• Chronic granulomatous disease (CGD)
• Combined variable immunodeficiency (CVID)
• Hemophagocytic lymphohistiocytosis (HLH)
• X-linked lymphoproliferative disease (XLP)
• X-linked severe combined immunodeficiency 1 (SCID-X1)
• Wiskott Aldrich Syndrome (WAS)

Metabolic Diseases

• Adrenoleukodystrophy (ALD)
• Globoid cell leukodystrophy (Krabbe disease)
• Hunter syndrome
• Hurler syndrome
• Metachromatic leukodystrophy
• Morquio syndrome
• Sanfillipo syndrome

Osteopetrosis

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• Stem cell transplants for metabolic disorders of the brain