‘Bubble Boy’ Disease, Nearly Always Fatal, Could Have a Cure
December 12, 2013
An international consortium of scientists is finding promising early results in a new gene therapy clinical trial they say may lead to an eventual long-term cure for SCID-X1, ABC News reports, Eight out of nine children given gene therapy in the study – all age 3 and younger and living around the world – are fighting off everyday germs that once might have killed them, according to research presented by Dana-Farber/Boston Children’s Cancer and Blood Disorders Center.
Read the full story. Read the news release.