Fighting genetic disease with help of HIV virus
October 23, 2016
A gene therapy trial in Italy led by Alessandra Biffi, MD, who now directs the Gene Therapy Program at Dana-Farber/Boston Children’s, has
had promising results treating children with a devastating inherited neurological
disorder called metachromatic leukodystrophy, CBS Sunday Morning reports.
disease strikes seemingly healthy children who then begin to lose most of their
capabilities and eventually succumb to the illness.