One boy’s cure raises hopes and questions about gene therapy for sickle cell disease

March 01, 2017

red blood cells

A closely watched study using gene therapy to treat sickle cell disease cured one patient, a boy in France, researchers reported in the New England Journal of Medicine, offering a glimmer of hope for a long-neglected disease but one that comes with several caveats, Stat and other outlets report in stories that feature comments from Dana-Farber/Boston Children’s researchers.

Read the Stat story. See also coverage from New Scientist, Health Day, the Associated Press and The Guardian.

Media Inquiries

Irene Sege
Senior Media Relations Specialist
irene.sege@childrens.harvard.edu
1-617-919-7379

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