Gene Therapy Trial for "Bubble Boy Syndrome"
August 23, 2013
Bubble Boy Syndrome is a rare, immune deficiency disease that makes baby boys vulnerable to simple afflictions like the common cold. Historically, these boys were only expected to live to one year of age, but that may change because of a groundbreaking new gene therapy treatment pioneered by an international coalition of scientists led in the United States by David Williams, MD. (Innovation Hub, WGBH radio).
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