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Vietnamese boy thrives after gene therapy for Wiskott-Aldrich syndrome

August 23, 2017
After being diagnosed with Wiskott-Aldrich syndrome, Duy Anh "Harry" Le traveled with his family to Boston for a gene therapy clinical trial, and is now a happy and healthy two-year-old.

Novel CRISPR-Cas9 genetic screening approach enables discovery of new drug targets to aid cancer immunotherapy

July 19, 2017
A novel screening method, using CRISPR-Cas9 genome editing technology to test the function of thousands of tumor genes in mice, has revealed new drug targets that could potentially enhance the effectiveness of PD-1 checkpoint inhibitors, a promising new class of cancer immunotherapy.

Dana-Farber/Boston Children's again named a top national pediatric cancer program

June 27, 2017
U.S. News & World Report has ranked Dana-Farber/Boston Children's Cancer and Blood Disorders Center the nation's #2 pediatric cancer program in its new 2017-18 Best Children's Hospitals report.

Gene Therapy 2.0

March 15, 2017
Levi Looks, diagnosed through newborn screening with “bubble boy” disease, is a healthy toddler thanks to gene therapy, resurgent now after early setbacks, MIT Technology Review reports.

How dogs may help fight bone cancer

March 12, 2017
In the growing field of comparative oncology, veterinarians are teaming up with oncologists to study the similarities in human and canine cancer to boost cure rates for people and pets alike, CBS Sunday Morning reports.

How a child made scientists think of cytokines as knobs instead of switches

March 09, 2017
An unusual case of a rare anemia is opening scientists up to a new way of thinking about how to adapt and employ cytokines, messenger molecules of the blood and immune system, as tools for treatment and to illustrate the promise of precision medicine, Harvard Gazette reports.

Martial arts instructors volunteer with kids fighting cancer

March 02, 2017
Karate and its ability to calm is proving to be a powerful combination to help children cope with cancer, WCVB-TV reports, in a story that features a young stem cell transplant patient.

One boy’s cure raises hopes and questions about gene therapy for sickle cell disease

March 01, 2017
Dana-Farber/Boston Children’s researchers, who are developing a gene therapy trial for sickle cell disease, commented in Stat and other outlets on a case report from a different trial.

The Lifesaving Care Act

February 27, 2017
A young woman, whose treatment at Dana-Farber/Boston Children’s for Hodgkin’s lymphoma included a stem cell transplant, tells Boston Globe columnist Kevin Cullen how the Affordable Care Act helped her.

From moving mountains to climbing mountains, Fulton native seeks to redefine ‘possible’

February 20, 2017
A young upstate New York man, blind since leukemia spread to his eyes, is preparing to climb Mount Kilamanjaro, Oswego County (NY) Today reports.
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